SMi's 7th annual Orphan Drugs and Rare Diseases UK Conference


SMi Group is thrilled to present the 7th annual Orphan Drugs and Rare Diseases conference, taking place on 18th & 19th October 2017 in Central London, UK. This year’s theme will be focused towards discussing strategies for patient engagement, market access and gene therapies to enhance rare diseases and orphan drug research.

Aimed at an audience of senior scientists and oncology specialists involved in targeting rare diseases therapies and drug research, Orphan Drugs UK 2017 will provide a perfect platform to discuss pioneering clinical developments and the next generation of clinical trial process. The 7th annual conference will capture expert insight through dedicated focus new therapies for different rare diseases, the importance of orphan drug development and reimbursement and repurposing.

Join us this October for strategic direction from the Rare Disease community and leverage your knowledge with the key requirements and tools for successful patient recruitment and retention through informed guidance delivered by a panel of industry experts.


Featured Speakers:

• Olivier Morand, Clinical Science Program Head, Actelion Pharmaceuticals
• Larissa Kerecuk, Rare Disease Lead, Consultant Paediatric Nephrologist, Birmingham Children’s Hospital
• Stuart Hughes, Director, Head of Pharmacology, Vertex
• Nadia Assenova, Senior Director Regulatory Affairs, EMEA, Alexion Pharma GmbH
• Christine Lavery, Group Chief Executive, MPS Society
• Olaf Ritzeler, External Innovation Lead, Sanofi
• Stephen Marcus, CEO, Cantex Pharmaceuticals
• Kei Kishimoto, Chief Scientific Officer, Selecta Biosciences




Exclusive highlights in 2017:

• Learn about new therapies for different rare diseases, and how these can successfully be applied to other diseases with similar attributes
• Hear what opportunities and challenges come with working on rare diseases, as well as the development of the world’s first rare disease centre for children
• Expand your knowledge on patient collaboration and patient centric models with the stream on patient engagement, covering improvement strategies, patient-led trials, and much more
• Gather further insight on drug approval and reimbursement with MAA, and how techniques for drug repurposing in the rare disease area can help treatment

Visitors

Previous attendees included:



Abeona Therapeutics; ADB Medical; Agency for Medicinal Products and Medical Devices of the Republic of Slovenia; Akcea Therapeutics; AKU Society; Alexion Pharma International Intl; Alexion Pharma International Sàrl; Alexion Pharma UK Ltd; Alexion Pharmaceuticals, Inc.; Apex Healthcare Consulting Limited; Birmingham Children's Hospital; Boehringer Mannheim GmbH; Cello Health Insight - London; Chiesi Farmaceutici SpA; Chiesi Ltd; Clarivate Analytics; Clinical Network Services (UK) Ltd; ClinTec International Ltd; Cydan; Debio Pharm S A; Diamond Pharma Services; Diamond PV Services; Dorphan; Findacure Development; Findacure; Genethon; Genetic Alliance; Grifols Deutschland; Grunenthal GmbH; GSK; GW Pharmaceuticals; Healx; I.D.E.A. Ltd; ICON Clinical Research; INC Research; Infusion Pharma Consulting LLC; Institute of Pharmaceutical Research & Technology (IFET SA); Loulou Foundation; Merck Serono; Mereo BioPharma Group Limited; MHRA; National Institute for Health and Care Excellence; NDA Regualtory Science Ltd; Newcastle University; Nicole Reichman; nspm UK ltd; Orphazyme ApS; Otsuka Europe Development and Commercialisation; Otsuka Pharmaceutical Europe Ltd; Personalize My Medicine; Pfizer Group; Premier Research; Proceutica; Prometic Pharma SMT; PSR Group B.V.; PSR Orphan Experts; Quintiles; Raglan Capital; Rare Base Ltd; Rare Disease UK; RBV Capital; RJW & Partners Ltd; Roche Products; Roche; Russian Respiratory Society; Shire Pharmaceuticals Limited; Society for Mucopolysaccharide Diseases; Summit Therapeutics; Swedish Orphan Biovitrum (SOBI) AB; Taylor & Francis Group; Taylor & Francis; The Birmingham Childrens Hospital; The Medical Research Network; The Ultra Rare Diseases Disorder & Disabilities Foundation; Thomson Reuters; Tikomed; University College London; URB Pharma; Vanda Pharmaceuticals; Zogenix Inc

Exhibitors

Past Exhibitors include:

Clinec International & Inc Research

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